Biomarin Pharmaceutical Inc Stock Price, News & Analysis

BioMarin Pharmaceutical Inc. (Nasdaq:BMRN) has appointed Maykin Ho, Ph.D., a former Goldman Sachs partner, to its Board of Directors. Dr. Ho brings over 30 years of experience in healthcare and finance, aimed at supporting BioMarin's growth in addressing rare genetic diseases. The Chairman and CEO, Jean-Jacques Bienaimé, expressed confidence in Dr. Ho's expertise to enhance the company's strategic direction. BioMarin continues to develop innovative therapies with a portfolio of six commercialized products and numerous candidates in various stages.

BioMarin Pharmaceutical Inc. (NASDAQ: BMRN) announced a conference call scheduled for February 25, 2021, at 4:30 p.m. ET. CEO Jean-Jacques Bienaimé will discuss the company's fourth quarter and full year 2020 financial results alongside a business update. The call can be accessed via a live audio webcast on the BioMarin website. For U.S. participants, the dial-in number is (866) 502-9859, while international participants can dial (574) 990-1362, using Conference ID 6488682.

BioMarin Pharmaceutical (BMRN) announced positive topline results from its Phase 3 GENEr8-1 study of valoctocogene roxaparvovec, a gene therapy for severe hemophilia A. The trial included 134 participants and found an 84% reduction in Annualized Bleeding Rate (ABR) after one year, with 80% of participants being bleed-free by week five. Factor VIII infusions also decreased by 99%. The FDA granted Breakthrough Therapy Designation, and BioMarin plans to submit data for marketing approval. The study represents a significant step toward a new treatment paradigm for hemophilia A.

BioMarin Pharmaceutical (NASDAQ: BMRN) has announced its participation in two upcoming virtual investor conferences. An audio webcast of these presentations will be available live, with access provided through the company's investor relations website. Additionally, an archived version will be accessible for a limited time post-conference. BioMarin specializes in innovative therapies for serious rare disorders, boasting a portfolio of six commercialized products along with several candidates in clinical stages.

BioMarin Pharmaceutical announced positive results from the Phase 3 extension study of vosoritide, a treatment for children with achondroplasia. Following two years of treatment, children showed maintained growth acceleration with a cumulative height gain of 3.52 cm compared to untreated subjects. The treatment was well tolerated, with 93% of participants remaining on it. Regulatory applications for vosoritide are under review by the FDA and EMA, with potential approval dates in August and the second half of 2021, respectively. This could mark the first therapy for achondroplasia in these regions.

BioMarin Pharmaceutical (NASDAQ: BMRN) announced its participation in two upcoming virtual investor conferences. An audio webcast of the presentations will be available for live access and later archived on the company's website. BioMarin focuses on developing innovative therapies for life-threatening rare disorders, boasting a portfolio that includes six commercialized products along with several clinical and pre-clinical candidates. For further details, please visit www.biomarin.com.

BioMarin Pharmaceutical (BMRN) announced a preclinical collaboration with Deep Genomics on November 17, 2020, to enhance drug discovery using AI technology. The partnership focuses on identifying oligonucleotide drug candidates for four rare diseases with significant unmet needs. Financial terms remain undisclosed, but Deep Genomics will receive an upfront payment and potential development milestones. This collaboration aims to leverage AI for faster identification and validation of therapeutic candidates, aiming to expedite BioMarin's development pipeline in rare disease treatments.

BioMarin Pharmaceutical (NASDAQ: BMRN) announced its participation in three upcoming virtual investor conferences on November 12, 2020. Management will be presenting, and an audio webcast will be available live on their website. Archived versions of the presentations will be accessible for a limited time post-conference. BioMarin focuses on developing innovative therapies for serious rare disorders and has a strong portfolio with six commercialized products and ongoing clinical candidates. Further details can be found on their official website.