Larimar Therapeutics, Inc. develops treatments for complex rare diseases, with its lead program, nomlabofusp, focused on Friedreich’s ataxia. Nomlabofusp is a subcutaneously administered recombinant fusion protein designed to deliver frataxin to mitochondria, and company updates frequently address clinical data, frataxin measurement, FDA interactions and regulatory designations tied to that program.
Recurring LRMR news also covers operating and financial results, equity financing activity, corporate presentations and research publications related to its intracellular delivery platform. The company’s disclosures connect program development with capital needs, rare-disease regulatory pathways and the broader use of fusion proteins for diseases involving intracellular bioactive-compound deficiencies.
Larimar Therapeutics (Nasdaq: LRMR), a clinical-stage biotechnology company, announced management participation in virtual 1x1 investor meetings at the Piper Sandler 33rd Annual Healthcare Conference from November 29 to December 2, 2021. The company is focused on developing treatments for complex rare diseases, particularly its lead compound CTI-1601, which is undergoing a Phase 1 clinical program for Friedreich's ataxia. Larimar aims to leverage its intracellular delivery platform to create new fusion proteins for additional rare diseases.
Larimar Therapeutics (Nasdaq: LRMR), a clinical-stage biotechnology company, announced its participation in 1x1 investor meetings at the Guggenheim Virtual Neuro/Immunology Conference on November 15-16, 2021. The company focuses on developing treatments for complex rare diseases, with its lead compound CTI-1601 currently in a Phase 1 clinical program targeting Friedreich's ataxia. Larimar aims to utilize its intracellular delivery platform for other fusion proteins aimed at rare diseases characterized by deficiencies in intracellular bioactive compounds.
Larimar Therapeutics, Inc. (Nasdaq: LRMR) reported its third quarter and year-to-date results as of September 30, 2021. The company has a strong balance sheet with $78 million in cash and marketable securities. Despite a clinical hold on its CTI-1601 program by the FDA due to safety concerns, they have compelling Phase 1 data and are focused on addressing Friedreich’s ataxia. The net loss for Q3 2021 was $16.8 million ($0.92 per share), increasing from $10.3 million in Q3 2020. R&D expenses rose to $14 million from $6.9 million in Q3 2020, driven by higher clinical supply costs.
LARIMAR Therapeutics, Inc. (Nasdaq: LRMR) announced participation in 1x1 investor meetings at the SVB Leerink CybeRx Series event focused on neuromuscular and rare diseases, scheduled for September 22-23, 2021. Larimar is a clinical-stage biotech company dedicated to developing treatments for complex rare diseases, with its lead compound, CTI-1601, undergoing Phase 1 clinical trials as a potential treatment for Friedreich's ataxia. The company aims to leverage its innovative intracellular delivery platform for future therapies targeting additional rare diseases.
Larimar Therapeutics (Nasdaq: LRMR), a clinical-stage biotechnology company, announced that Carole Ben-Maimon, MD, will present at the Morgan Stanley 19th Annual Global Healthcare Conference from September 9-15, 2021. The event features 1x1 investor meetings and will include a fireside chat on September 9 at 5:00 PM ET. Larimar is focused on developing treatments for complex rare diseases, notably its lead compound CTI-1601 for Friedreich's ataxia, currently in Phase 1 clinical trials in the U.S.
BALA CYNWYD, Pa., Aug. 19, 2021 – Larimar Therapeutics, Inc. (Nasdaq: LRMR) announced that Dr. David Bettoun will present at the World Orphan Drug Congress USA 2021 on August 27. His presentation, titled 'Expanding Therapeutic Possibilities for Rare Diseases,' will showcase preclinical in vitro data on Larimar's proprietary protein replacement therapy platform. Larimar is focused on developing treatments for rare diseases, with its lead compound, CTI-1601, currently in Phase 1 trials for Friedreich's ataxia.
Larimar Therapeutics (LRMR) reported positive Phase 1 results for CTI-1601, demonstrating proof-of-concept in Friedreich’s ataxia patients. Subcutaneous doses (50 mg and 100 mg) achieved frataxin levels comparable to normal heterozygous carriers. Safety data revealed no serious adverse events. As of June 30, 2021, the company had $70.6 million in cash. A $20 million equity financing was closed on July 2, 2021. However, the FDA placed a clinical hold on the CTI-1601 program due to mortalities in a toxicology study, requiring further data for trial resumption.
Larimar Therapeutics (Nasdaq: LRMR) announced that CEO Carole Ben-Maimon will participate in the William Blair Biotech Focus Conference 2021, scheduled virtually for July 14-15. Dr. Ben-Maimon will engage in a fireside chat on July 15 at 3:00 PM ET, discussing the company's development of treatments for complex rare diseases. Larimar's lead candidate, CTI-1601, is being evaluated for Friedreich's ataxia in a Phase 1 program. A replay of the chat will be accessible on Larimar's website.
Larimar Therapeutics (Nasdaq: LRMR) announced that CEO Carole Ben-Maimon will present at the JMP Securities Life Sciences Conference on June 16-17, 2021. The presentation will take the form of a fireside chat scheduled for 2:00 PM ET on June 16. Larimar focuses on developing treatments for rare diseases, currently evaluating its lead compound, CTI-1601, in a Phase 1 clinical program for Friedreich’s ataxia. The company aims to utilize its platform for creating fusion proteins targeting additional rare diseases.
Larimar Therapeutics (Nasdaq: LRMR) announced a clinical hold by the FDA on its CTI-1601 program due to mortalities observed in a non-human primate toxicology study. The company will not proceed with its planned private placement financing. CEO Carole Ben-Maimon emphasized patient safety and confirmed ongoing evaluation of data to comply with FDA requirements, potentially delaying upcoming trials into 2022. Larimar has $81.4 million in cash, sufficient for operations through mid-2022, and continues to believe in a viable path for CTI-1601’s development.