Ptc Therapeutics Stock Price, News & Analysis

PTC Therapeutics (NASDAQ: PTCT) presented its R&D pipeline updates and commercial progress at the J.P. Morgan Healthcare Conference on January 11, 2021. Highlights from 2020 include a DMD franchise revenue of approximately $331 million, with significant contributions from Translarna and Emflaza. The company anticipates 2021 revenues between $355 and $375 million for the DMD franchise and plans to conduct several clinical trials. Preliminary financial results indicate approximately $1.1 billion in cash and equivalents by year-end 2020.

PTC Therapeutics announced its participation in the 39th Annual J.P. Morgan Healthcare Conference on January 11, 2021, at 7:30 a.m. EST. The event will be webcast live, with a replay available for 30 days. The company focuses on developing and commercializing innovative medicines for rare disorders, aiming to improve patient access to necessary treatments. Interested parties are encouraged to join the webcast via the investor relations section on PTC's website.

PTC Therapeutics (NASDAQ: PTCT) announced the approval of non-statutory stock options for 12,500 shares and 4,360 restricted stock units (RSUs) to 10 new employees as part of their employment compensation. These awards were granted under NASDAQ's inducement grant exception on December 15, 2020. The stock options have an exercise price of $66.37 and will vest over four years. The RSUs will follow a similar vesting schedule. PTC, focused on rare disorders, continues to strengthen its workforce to support its mission in biopharmaceutical development.

PTC Therapeutics will host a webinar on December 15, 2020, at 12:00 noon ET, focusing on Translarna, a treatment for nonsense mutation Duchenne muscular dystrophy (nmDMD). The session will discuss clinical and real-world data, commercial success, and potential regulatory milestones in the United States. Results from Study PTC124-GD-045-DMD are expected in Q1 2021. The webinar can be accessed via phone or through the company's website, with a replay available for 30 days.

PTC Therapeutics (NASDAQ: PTCT) announced on December 2, 2020, the approval of stock options and restricted stock units (RSUs) for 47 new employees as part of their compensation package. The grant includes 41,955 stock options at an exercise price of $63.86 and 20,735 RSUs, both vesting over four years. These inducement grants comply with NASDAQ Listing Rule 5635(c)(4) and were approved by the Compensation Committee to attract new talent.

PTC Therapeutics announced that Translarna (ataluren) has received marketing approval in the Russian Federation for treating nonsense mutation Duchenne muscular dystrophy (nmDMD), impacting an estimated 13% of DMD patients. This approval is significant as Translarna is the only medicine targeted at the underlying cause of nmDMD in approved regions. CEO Stuart W. Peltz highlighted the demand from Russian physicians and the identification of nmDMD patients who may benefit. This marks an important milestone in PTC's goal to globally provide access to this treatment.

PTC Therapeutics (NASDAQ: PTCT) has initiated the registration-directed Phase 3 MOVE-FA study for vatiquinone (PTC743) in children and young adults with Friedreich ataxia (FA), a rare neurodegenerative disorder. This pivotal trial comes after vatiquinone showed positive results in a Phase 2 trial, impacting disease severity over 24 months. The trial will enroll approximately 110 participants across multiple regions, with primary endpoints focused on the modified Friedreich ataxia rating scale. The FDA has granted vatiquinone both Orphan Drug and Fast Track Designations.

PTC Therapeutics (NASDAQ: PTCT) will present at the Evercore ISI 3rd Annual HealthCONx Conference on December 1, 2020, at 11:45 a.m. ET. This presentation, featuring a company overview, will be available via live webcast on PTC's website, with an archived version accessible for 30 days. PTC Therapeutics is a global biopharmaceutical company specializing in innovative treatments for rare disorders, emphasizing its commitment to meeting unmet medical needs through a diversified pipeline of transformative medicines.

PTC Therapeutics has received multiple designations from the U.S. FDA for its drug PTC596, intended for treating rare cancers: leiomyosarcoma (LMS) and Diffuse Intrinsic Pontine Glioma (DIPG). These include Orphan Drug and Fast Track designations for LMS and both Orphan Drug and Rare Pediatric Disease designations for DIPG. PTC596, currently in clinical trials, shows potential in targeting and inhibiting cancer cell growth. Each year, around 4,000 LMS and 300 DIPG cases are diagnosed in the U.S., highlighting the critical need for effective treatments in these areas.