Ultragenyx Pharm Stock Price, News & Analysis

Ultragenyx (NASDAQ: RARE) will host a conference call at 5:00 p.m. ET on Tuesday, November 4, 2025 to discuss third quarter 2025 financial results and a corporate update for the period ended September 30, 2025.

The live webcast and replay will be available at https://ir.ultragenyx.com/events-presentations. The replay will remain available for three months.

Ultragenyx (NASDAQ: RARE) reported an inducement grant of 20,317 restricted stock units (RSUs) to 17 newly hired non-executive officers, approved by the compensation committee and granted under the Ultragenyx Employment Inducement Plan.

The grant date was October 16, 2025 and the awards were disclosed October 24, 2025 as material inducements under Nasdaq Listing Rule 5635(c)(4). The RSUs vest over four years with 25% vesting on each anniversary, contingent on continuous employment.

Ultragenyx (NASDAQ: RARE) reported an inducement equity grant under Nasdaq Listing Rule 5635(c)(4) for a newly hired non-executive officer, with a grant date of September 30, 2025.

The company granted 62,232 non-qualified stock options and 34,564 restricted stock units. The options have a ten-year term and an exercise price of $30.08, equal to the closing price on September 30, 2025. RSUs vest 25% annually over four years; options vest 25% after one year then monthly over the remaining three years (1/48th monthly), subject to continued employment.

Ultragenyx Pharmaceutical (NASDAQ: RARE) has appointed Eric Olson as Chief Business Officer and Executive Vice President, effective September 22, 2025. Olson succeeds Thomas Kassberg, who is retiring after 14 years with the company.

Olson brings nearly two decades of biopharma industry experience, having led or supported transactions worth over $15 billion. His previous roles include CBO at Stoke Therapeutics, VP of Business Development at Alnylam Pharmaceuticals, and leadership positions at Takeda and Genzyme Corporation. Notable deals include Stoke's partnership with Biogen and Alnylam's $2.8 billion collaboration with Roche.

In his new role, Olson will lead Ultragenyx's business development, corporate development, and alliance management functions, supporting the company's mission to develop therapies for untreated rare diseases.

Ultragenyx Pharmaceutical (NASDAQ: RARE), a biopharmaceutical company specializing in rare and ultra-rare disease therapies, has announced an inducement grant of 48,561 restricted stock units to 17 newly hired non-executive officers. The grants were approved by the company's compensation committee under the Ultragenyx Employment Inducement Plan on September 16, 2025.

The restricted stock units feature a four-year vesting schedule, with 25% of shares vesting annually on the grant date anniversary, contingent on continued employment. This grant complies with Nasdaq Listing Rule 5635(c)(4) for employment inducement awards.

Ultragenyx Pharmaceutical (NASDAQ: RARE) announced positive 96-week results from its Phase 3 study of DTX401, a gene therapy for glycogen storage disease type Ia (GSDIa). The therapy demonstrated significant improvements in reducing cornstarch dependency while maintaining glycemic control.

Key findings at Week 96 include a 61% mean reduction in daily cornstarch intake for both treatment and crossover groups, with 70-75% reduction in nighttime cornstarch usage. Two-thirds of participants eliminated at least one nighttime dose. The therapy's efficacy was further validated by data from a Japanese cohort, where all three pediatric participants achieved 95% reduction in cornstarch intake by Week 24, with complete elimination in all cases.

Patient quality of life improved significantly, with 83-95% of participants reporting reduced disease burden. The treatment demonstrated an acceptable safety profile with manageable hepatic reactions.

Ultragenyx Pharmaceutical (NASDAQ: RARE), a biopharmaceutical company specializing in rare and ultra-rare genetic disease therapies, has announced its participation in three major investor conferences in September 2025.

The company's leadership, including Chief Medical Officer Eric Crombez, M.D. and Chief Financial Officer Howard Horn, will participate in fireside chats and host one-on-one meetings at the Cantor Global Healthcare Conference (September 4), Morgan Stanley Global Healthcare Conference (September 9), and Bank of America Global Healthcare Conference (September 23). All fireside chat sessions will be available via webcast on the company's investor relations website.

Ultragenyx Pharmaceutical (NASDAQ: RARE), a biopharmaceutical company specializing in rare and ultra-rare disease therapies, has announced an inducement grant of 113,572 restricted stock units to 33 newly hired non-executive officers. The grants, approved by the company's compensation committee, were made under the Ultragenyx Employment Inducement Plan on August 16, 2025.

The restricted stock units will vest over a four-year period, with 25% of shares vesting annually on each grant date anniversary, contingent on continuous employment.

Ultragenyx Pharmaceutical (NASDAQ: RARE) has initiated a rolling submission of a Biologics License Application (BLA) to the FDA for DTX401, their AAV gene therapy treatment for Glycogen Storage Disease Type Ia (GSDIa). The company has submitted the non-clinical and clinical modules and plans to complete the full BLA with the chemistry, manufacturing and controls (CMC) module in Q4 2025.

The BLA includes 96-week Phase 3 study data showing significant cornstarch reduction in patients: 60% reduction in the ongoing DTX401 group and 64% reduction in the Crossover Placebo to DTX401 group. The submission will address FDA observations from the UX111 complete response letter regarding CMC and manufacturing facilities.