Welcome to our dedicated page for Rocket Pharmaceu news (Ticker: RCKT), a resource for investors and traders seeking the latest updates and insights on Rocket Pharmaceu stock.
Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) is a fully integrated, late-stage biotechnology company developing investigational genetic therapies for rare and often life-threatening disorders. The RCKT news feed on Stock Titan aggregates company announcements, press releases and third-party coverage related to its AAV and lentiviral gene therapy programs.
Investors following Rocket’s news can track updates on its adeno-associated viral (AAV) cardiovascular portfolio, which includes RP-A501 for Danon disease, RP-A601 for PKP2-arrhythmogenic cardiomyopathy (PKP2-ACM) and RP-A701 for BAG3-associated dilated cardiomyopathy (BAG3-DCM). News items frequently cover clinical trial milestones, such as FDA lifting a clinical hold on the pivotal Phase 2 trial of RP-A501, preliminary Phase 1 data for RP-A601, and IND clearance and Fast Track designation for RP-A701.
The news stream also highlights developments in Rocket’s lentiviral (LV) hematology portfolio, including regulatory progress for KRESLADI (marnetegragene autotemcel; marne-cel) in severe leukocyte adhesion deficiency-I (LAD-I). Articles may discuss FDA acceptance of the resubmitted Biologics License Application (BLA), the setting of a Prescription Drug User Fee Act (PDUFA) target action date, and clinical data showing survival and infection outcomes in treated patients.
Beyond pipeline updates, RCKT news includes financial results, strategic corporate reorganization and pipeline prioritization announcements, leadership and board changes, equity inducement grants and participation in major healthcare investor conferences. By reviewing this page regularly, readers can follow how Rocket’s clinical, regulatory and corporate events may influence sentiment around RCKT stock and gain context on the company’s progress in gene therapy for rare cardiovascular and hematologic diseases.
Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) reported positive results from its Phase 2 trial for RP-L201, a gene therapy for severe Leukocyte Adhesion Deficiency-I (LAD-I). The trial demonstrated 100% overall survival at one year post-infusion and significant clinical improvement in patients. All nine patients showed sustained CD18 expression with no serious adverse events. Rocket plans to engage health authorities for regulatory filings anticipated in the first half of 2023, focusing on the therapy's potential to transform treatment options for LAD-I.
Rocket Pharmaceuticals (NASDAQ: RCKT) recently announced promising clinical updates from its ongoing gene therapy trials. The Phase 1 trial for RP-A501 in Danon Disease showed the treatment was well-tolerated in pediatric patients with no reported toxicities. In the Phase 2 trial for Fanconi Anemia, five out of nine patients exhibited sustained increased resistance to mitomycin-C, achieving the trial's primary endpoint. Additionally, treatments for Pyruvate Kinase Deficiency demonstrated normalized hemoglobin levels in patients 18 months post-infusion.
Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) is set to present at the UBS Global Healthcare Conference on May 24 at 7:45 a.m. ET in New York. CEO Gaurav Shah will deliver the presentation, with a live audio webcast available on the company's website. Rocket focuses on developing genetic therapies for rare childhood disorders, including Fanconi Anemia, Leukocyte Adhesion Deficiency-I, and Pyruvate Kinase Deficiency. The company employs a platform-agnostic approach to offer innovative treatment options, addressing significant unmet needs in pediatric healthcare.
Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) reported a net loss of $43M, or $0.67 per share, for Q1 2022. The company holds $346.6M in cash, extending its operational runway into H1 2024. Key updates include the advancement of four clinical programs targeting Danon Disease, Fanconi Anemia, Leukocyte Adhesion Deficiency-I, and Pyruvate Kinase Deficiency, with data readouts expected throughout 2022. Significant leadership appointments were made, including Fady Malik, M.D., to the Board and Carlos Martin as Chief Commercial Officer. The company also anticipates AAV cGMP manufacturing readiness in Q2 2022.
Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) is set to present at the Bank of America Securities Healthcare Conference on May 11 at 2:20 p.m. ET. The company specializes in developing genetic therapies for rare childhood disorders, including Fanconi Anemia and Danon Disease. Rocket utilizes a platform-agnostic approach, focusing on tailored therapy solutions. Given the ongoing impact of COVID-19, the company emphasizes the safety and effectiveness of its product candidates, while also addressing potential delays in clinical trials.
Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) announces key upcoming presentations: President Kinnari Patel will present at the Guggenheim 3rd Annual Genomic Medicines and Rare Disease Conference on April 1 at 8:00 a.m. ET, and CEO Gaurav Shah will speak at the 21st Annual Needham Virtual Healthcare Conference on April 11 at 10:15 a.m. ET. The live webcasts will be accessible on the company's website, with replays available post-event. Rocket focuses on genetic therapies for rare childhood disorders, including Fanconi Anemia and Danon Disease.
Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) has appointed Fady Malik, M.D., Ph.D., to its Board of Directors. Dr. Malik, with nearly 25 years of experience as a cardiovascular physician-scientist and biopharmaceutical executive, will serve as an independent non-executive director. CEO Gaurav Shah emphasized Dr. Malik's expertise in R&D and leadership in bringing medicines from research to clinical application, particularly in cardiology. Rocket is advancing its clinical pipeline for rare childhood disorders, including Danon Disease, and aims for agency alignment on its Phase 2 clinical study.
Rocket Pharmaceuticals (NASDAQ: RCKT) has appointed Jessie Yeung as Vice President of Investor Relations and Corporate Finance. With over 15 years of experience, including a previous role at Legend Biotech (NASDAQ: LEGN), Yeung will lead investor relations and capital market strategies. CEO Gaurav Shah emphasized Yeung's expertise will enhance communication with investors as the company approaches significant milestones in gene therapy clinical programs.
Rocket Pharmaceuticals, focusing on genetic therapies for rare childhood disorders, announced positive Phase 1 results for Danon Disease, showing clinical benefits in four adults. The data indicated sustained improvement across clinical metrics. In pivotal Phase 2 trials for LAD-I, nine patients exhibited successful engraftment, with CD18 expression ranging from 26% to 87%. Six out of eight patients in the Fanconi Anemia trial demonstrated engraftment, with data expected soon. The company holds a strong cash position of $388.7 million, ensuring operational funding into the second half of 2023.
Rocket Pharmaceuticals (NASDAQ: RCKT), a clinical-stage company focused on genetic therapies for rare childhood disorders, has announced that CEO Gaurav Shah will participate in a virtual fireside chat at the 11th Annual SVB Leerink Global Healthcare Conference on February 16 at 10 a.m. ET. Investors can access a live audio webcast of the presentation on the company's website. Rocket's pipeline includes therapies for conditions such as Fanconi Anemia and Danon Disease, utilizing both lentiviral and adeno-associated viral vector approaches.
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