Welcome to our dedicated page for Vertex Pharmaceuticals news (Ticker: VRTX), a resource for investors and traders seeking the latest updates and insights on Vertex Pharmaceuticals stock.
Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) is a global biotechnology company with approved medicines in cystic fibrosis, sickle cell disease, transfusion-dependent beta thalassemia and acute pain, and a broad pipeline across kidney disease, neuropathic pain, type 1 diabetes and other serious conditions. The VRTX news feed on Stock Titan brings together company press releases and other coverage that highlight how its commercial portfolio and research programs are evolving over time.
News about Vertex often focuses on clinical data readouts, regulatory milestones and commercial updates. Recent announcements have covered progress in cystic fibrosis, including data on ALYFTREK and other CFTR modulators presented at scientific conferences, and updates on next-generation CFTR correctors and CFTR mRNA therapies. Vertex also regularly reports on CASGEVY, its CRISPR/Cas9 gene-edited cell therapy for severe sickle cell disease and transfusion-dependent beta thalassemia, including longer-term outcomes data and plans for regulatory submissions in additional age groups.
Investors and followers of VRTX news can also expect updates on JOURNAVX, the company’s oral non-opioid NaV1.8 inhibitor for moderate-to-severe acute pain in adults, including information on prescription trends, payer coverage and hospital formulary adoption. In kidney diseases, Vertex issues news on povetacicept and inaxaplin, including Phase 1/2 and Phase 3 trial data in IgA nephropathy, primary membranous nephropathy and APOL1-mediated kidney disease, as well as regulatory designations such as Breakthrough Therapy and Fast Track.
Additional news items may include financial results, participation in major healthcare investor conferences, and updates on programs in type 1 diabetes, autosomal dominant polycystic kidney disease and myotonic dystrophy type 1. For anyone tracking VRTX stock, this news page offers a centralized view of how Vertex’s marketed products and pipeline advance through clinical development, regulatory review and commercialization.
Vertex Pharmaceuticals (VRTX) and Entrada Therapeutics (TRDA) have announced a global collaboration to develop intracellular EEV therapeutics for myotonic dystrophy type 1 (DM1). Entrada will receive an upfront payment of
Vertex Pharmaceuticals (NASDAQ: VRTX) will participate in key investor conferences including the Jefferies London Healthcare Conference on November 16, 2022, at 9:10 a.m. GMT and the 5th Annual Evercore ISI HealthCONx Conference on November 30, 2022, at 9:15 a.m. EST. Live webcasts of these events will be accessible on Vertex's website. Established in 1989, Vertex focuses on innovative treatments for serious diseases, particularly cystic fibrosis, and has a promising pipeline addressing various serious conditions. For more information, visit www.vrtx.com.
Vertex Pharmaceuticals (NASDAQ: VRTX) has partnered with basketball Hall-of-Famer Alonzo Mourning to launch the "Power Forward" initiative. This educational campaign aims to raise awareness about APOL1-mediated kidney disease (AMKD), emphasizing the significance of early diagnosis and genetic testing. AMKD affects approximately 100,000 individuals in the U.S. and is genetically driven, particularly impacting those of sub-Saharan African ancestry. The initiative offers resources to help at-risk individuals discuss kidney health with healthcare providers.
Vertex Pharmaceuticals (NASDAQ: VRTX) reports promising long-term data on TRIKAFTA® (elexacaftor/tezacaftor/ivacaftor), showcased at the North American Cystic Fibrosis Conference. The ongoing 192-week study shows sustained improvements in lung function and respiratory symptoms among patients with at least one F508del allele. In children aged 2-5, TRIKAFTA improved lung function and was generally well-tolerated. Vertex plans to submit regulatory applications for this age group. The latest findings reinforce TRIKAFTA's critical role in CF treatment.
Vertex Pharmaceuticals reported Q3 2022 product revenues of $2.33 billion, marking an 18% increase from Q3 2021. The company raised its full-year 2022 product revenue guidance to $8.8 billion to $8.9 billion, driven by strong uptake of TRIKAFTA/KAFTRIO. Net income increased by 9% to $931 million, with a diluted EPS of $3.59. Vertex continues to advance its clinical pipeline, including exa-cel for Sickle Cell Disease and VX-548 for acute pain, while increasing R&D investments.
Vertex Pharmaceuticals (NASDAQ: VRTX) will report its Q3 2022 financial results on October 27, 2022, after market close. A conference call is scheduled for 4:30 p.m. ET to discuss these results, accessible via phone and live webcast on Vertex's website.
Vertex is a leader in biotechnology, focusing on transformative medicines for serious diseases, particularly cystic fibrosis, and has a robust pipeline addressing other conditions like sickle cell disease and type 1 diabetes. The company is recognized as a top employer in the industry.
Vertex Pharmaceuticals (NASDAQ: VRTX) has initiated a first-in-human trial for VX-634, a new AAT corrector for alpha-1 antitrypsin deficiency (AATD). The FDA has approved the IND application for VX-634, marking a significant advancement in the company's AATD program. Alongside this, Vertex plans to launch a 48-week Phase 2 study of VX-864 to evaluate its long-term efficacy in reducing liver polymer levels and increasing functional AAT in plasma. The company will also introduce additional AAT correctors starting in 2023.
Vertex Pharmaceuticals and CRISPR Therapeutics have announced a rolling review of exa-cel by the U.S. FDA for treating sickle cell disease (SCD) and transfusion-dependent beta thalassemia (TDT), with submission starting in November 2022 and completion expected by Q1 2023. Submissions to the EMA and MHRA are also on track for Q4 2022. Exa-cel received multiple designations, including Fast Track and Orphan Drug status. The therapy aims to edit patients' stem cells for improved disease outcomes.
Vertex Pharmaceuticals (NASDAQ: VRTX) appointed Jonathan Biller as Chief Legal Officer effective September 19, 2022. Biller joins from Agios, where he held multiple executive roles, including Chief Financial Officer. Dr. Reshma Kewalramani, CEO, expressed excitement about Biller's depth of legal and industry experience, expecting him to support Vertex’s growth in cystic fibrosis and other disease treatments. Vertex continues to develop innovative therapies for serious diseases, including sickle cell disease and type 1 diabetes.
Vertex Pharmaceuticals has received FDA approval for the expanded use of ORKAMBI (lumacaftor/ivacaftor) to treat children aged 12 to under 24 months with cystic fibrosis who possess two copies of the F508del mutation. This represents the first time a treatment is available for this age group suffering from the underlying disease. This approval is founded on a recent Phase 3 study showing ORKAMBI's safety and potential to modify the disease's progression. ORKAMBI was first approved in 2015 and is currently available in over 30 countries.