Welcome to our dedicated page for Vertex Pharmaceuticals news (Ticker: VRTX), a resource for investors and traders seeking the latest updates and insights on Vertex Pharmaceuticals stock.
Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) is a global biotechnology company with approved medicines in cystic fibrosis, sickle cell disease, transfusion-dependent beta thalassemia and acute pain, and a broad pipeline across kidney disease, neuropathic pain, type 1 diabetes and other serious conditions. The VRTX news feed on Stock Titan brings together company press releases and other coverage that highlight how its commercial portfolio and research programs are evolving over time.
News about Vertex often focuses on clinical data readouts, regulatory milestones and commercial updates. Recent announcements have covered progress in cystic fibrosis, including data on ALYFTREK and other CFTR modulators presented at scientific conferences, and updates on next-generation CFTR correctors and CFTR mRNA therapies. Vertex also regularly reports on CASGEVY, its CRISPR/Cas9 gene-edited cell therapy for severe sickle cell disease and transfusion-dependent beta thalassemia, including longer-term outcomes data and plans for regulatory submissions in additional age groups.
Investors and followers of VRTX news can also expect updates on JOURNAVX, the company’s oral non-opioid NaV1.8 inhibitor for moderate-to-severe acute pain in adults, including information on prescription trends, payer coverage and hospital formulary adoption. In kidney diseases, Vertex issues news on povetacicept and inaxaplin, including Phase 1/2 and Phase 3 trial data in IgA nephropathy, primary membranous nephropathy and APOL1-mediated kidney disease, as well as regulatory designations such as Breakthrough Therapy and Fast Track.
Additional news items may include financial results, participation in major healthcare investor conferences, and updates on programs in type 1 diabetes, autosomal dominant polycystic kidney disease and myotonic dystrophy type 1. For anyone tracking VRTX stock, this news page offers a centralized view of how Vertex’s marketed products and pipeline advance through clinical development, regulatory review and commercialization.
Vertex Pharmaceuticals (NASDAQ: VRTX) announced participation in a fireside chat at the Wells Fargo Healthcare Conference on September 9, 2022, at 11:00 a.m. ET.
A live webcast of the event will be available on the company's website under the 'Investors' section. Vertex is a biotechnology company focusing on transformative medicines for serious diseases, notably cystic fibrosis, and has a strong pipeline addressing various genetic and chronic conditions.
Vertex Pharmaceuticals reported strong Q2 2022 results with product revenues of $2.20 billion, marking a 22% increase year-over-year. The company raised its full-year revenue guidance to $8.6 to $8.8 billion. Key drivers include the strong adoption of TRIKAFTA/KAFTRIO, particularly in the U.S., and advancements in multiple clinical programs for diseases like sickle cell and type 1 diabetes. Net income rose significantly to $810 million, or $3.13 per diluted share. Vertex's pipeline boasts late-stage clinical developments, promising a substantial growth trajectory.
Vertex Pharmaceuticals announced the advancement of VX-548, a selective NaV1.8 inhibitor, into Phase 3 clinical trials for acute pain management, slated to begin in Q4 2022. This follows positive results from the Phase 2 trials. The FDA has granted Breakthrough Therapy Designation to VX-548 for treating moderate to severe acute pain. The Phase 3 program will include two randomized studies focused on pain relief after surgeries and a third study assessing its efficacy across various pain types.
Vertex Pharmaceuticals (NASDAQ: VRTX) is set to release its second quarter 2022 financial results on August 4, 2022, post-market. A conference call will take place at 4:30 p.m. ET to discuss these results. Investors can access the call by dialing (877) 270-2148 or using international dial-in +1 (412) 902-6510. The event will also be webcast live on Vertex's website. Known for innovative treatments for cystic fibrosis, Vertex is expanding its pipeline to include therapies for other serious diseases like sickle cell disease and type 1 diabetes.
Vertex Pharmaceuticals announced a definitive agreement to acquire ViaCyte for $320 million in cash. This acquisition aims to enhance Vertex's efforts in developing VX-880, a stem cell-derived therapy for type 1 diabetes (T1D), which has shown promising results in clinical trials. The integration of ViaCyte's technologies, stem cell lines, and manufacturing capabilities is expected to accelerate Vertex’s T1D programs. The deal is anticipated to close later this year, pending standard regulatory conditions.
Vertex Pharmaceuticals has announced that the FDA has lifted the clinical hold on its Phase 1/2 trial for VX-880, a stem cell therapy aimed at treating type 1 diabetes (T1D) in patients with impaired hypoglycemic awareness. The trial will resume screening and enrollment at multiple U.S. sites. Currently, three patients have been dosed, with further evaluation planned for five more in the next trial phase. VX-880 aims to restore insulin-producing islet cell function, addressing a crucial need in T1D treatment where existing options are limited.
Vertex Pharmaceuticals and CRISPR Therapeutics unveiled promising new data on exa-cel for treating transfusion-dependent beta thalassemia and severe sickle cell disease. The study involved 75 patients, with up to 37.2 months of follow-up. Key findings include:
- 42 out of 44 patients with beta thalassemia were transfusion-free post-treatment.
- All 31 patients with sickle cell disease experienced cessation of vaso-occlusive crises.
The safety profile aligns with myeloablative conditioning and stem cell transplant protocols.
Vertex Pharmaceuticals presented five abstracts on cystic fibrosis (CF) treatments at the ECFS 45th European Cystic Fibrosis Conference from June 8-11, 2022, in Rotterdam. Key findings from a study involving over 16,000 CF patients treated with TRIKAFTA showed significant improvements in lung function and a 77% reduction in pulmonary exacerbations. Additionally, early initiation of KALYDECO demonstrated better lung function preservation in children aged 6-10. These results underline the importance of early and continuous CFTR modulator therapy.
Vertex Pharmaceuticals (NASDAQ: VRTX) will participate in a fireside chat at the Goldman Sachs 43rd Annual Global Healthcare Conference on June 15, 2022, at 1:20 p.m. PT. A live webcast will be available on Vertex's website in the 'Investors' section. Vertex is a biotechnology company focused on creating transformative medicines, especially for cystic fibrosis (CF), and has an extensive pipeline targeting diseases like sickle cell disease and type 1 diabetes. The company has received recognition for its workplace culture and innovation.
Vertex Pharmaceuticals has received Breakthrough Therapy Designation from the FDA for inaxaplin (VX-147) targeting APOL1-mediated focal segmental glomerulosclerosis (FSGS). Additionally, the European Medicines Agency awarded PRIME designation for inaxaplin to treat APOL1-mediated chronic kidney disease (AMKD). Inaxaplin is the first therapy aimed at the underlying cause of AMKD. Vertex now holds nine Breakthrough Therapy Designations in the U.S., including three non-oncological PRIME designations.